Feb 9 (Reuters) - Regenxbio said on Monday the U.S. Food and Drug Administration had declined to approve its gene therapy for ...

After facing a delayed decision deadline and a clinical hold, Regenxbio’s Hunter syndrome gene therapy has been rejected by ...

Life Biosciences is pushing cellular rejuvenation into the clinic with ER-100, an experimental gene ...

The FDA in July last year declined to approve UX111 for Sanfilippo syndrome, a rare neurodegenerative disorder, citing ...

The Food and Drug Administration has rejected a rare-disease gene therapy from Regenxbio, the company said Monday.

The Food and Drug Administration paused trials for two experimental gene therapies from Regenxbio after one child developed a ...

Dr. Rebecca Ahrens-Nicklas and Dr. Kiran Musunru crafted a bespoke treatment that has successfully corrected the genetic ...

Gene therapy is a medical treatment that works by changing or fixing a person's genes to treat or prevent disease ...

Gene therapy holds the promise of preventing and curing disease by manipulating gene expression within a patient's cells.

Gene-editing tools like CRISPR have unlocked new treatments for previously uncurable diseases. Now, researchers at the ...

(Yicai) Jan. 28 -- Chinese medical researchers have made a breakthrough in gene therapy that overcomes the limitations of ...

A research team has successfully demonstrated the world's first gene-editing treatment for Leber's hereditary optic ...